BENITIONSClinical Trial Intelligence

Study to Evaluate Safety and Efficacy of VX-661 in Combination With Ivacaftor in Subjects With Cystic Fibrosis, Homozygous for the F508del-CFTR Mutation With an Open-Label Expansion

Phase 2 Completed NCT02070744

ConditionCystic Fibrosis
PhasePhase 2
SponsorVertex Pharmaceuticals Incorporated
StatusCompleted
Enrollment40 participants
InterventionsVX-661, Ivacaftor, Placebo matched to VX-661, Placebo matched to Ivacaftor
Start dateMar, 2014
Completion dateMay 27, 2016
Results postedApr 13, 2018

Summary

The objective of this study was to evaluate the safety and efficacy of VX-661in combination with ivacaftor in participants with cystic fibrosis (CF) who are homozygous for F508del cystic fibrosis transmembrane conductance regulator (CFTR) mutation

PC Phase: Number of Participants With Treatment-Emergent Adverse Events (AEs) and Serious Adverse Events (SAEs)

Baseline (PC Phase) up to 112 days · Participants

PC Phase: VX-661 50 mg q12h + IVA 150 mg q12h6 Participants
PC Phase: VX-661 Placebo q12h + IVA Placebo q12h5 Participants
PC Phase: VX-661 100 mg qd + IVA 150 mg q12h15 Participants
PC Phase: VX -661 Placebo qd + IVA Placebo q12h13 Participants
PC Phase: VX-661 50 mg q12h + IVA 150 mg q12h1 Participants
PC Phase: VX-661 Placebo q12h + IVA Placebo q12h2 Participants

OLE Phase: Number of Participants With Treatment-Emergent AEs and SAEs

Baseline (OLE Phase) up to 364 days · Participants

OLE Phase: VX-661 100 mg qd + IVA 150 mg q12h25 Participants
OLE Phase: VX-661 100 mg qd + IVA 150 mg q12h6 Participants

Open in BENITIONS View on ClinicalTrials.gov

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