BENITIONSClinical Trial Intelligence

First-in-human Study of SAR443579 Infusion in Male and Female Children and Adult Participants With Relapsed or Refractory Acute Myeloid Leukemia (R/R AML), B-cell Acute Lymphoblastic Leukemia (B-ALL), High Risk-myelodysplasia (HR-MDS), or Blastic Plasmacytoid Dendritic Cell Neoplasm (BPDCN)

Phase 1/2 Terminated NCT05086315

ConditionAcute Lymphocytic Leukaemia, Acute Myeloid Leukaemia Refractory, Myelodysplastic Syndromes, Blastic Plasmacytoid Dendritic Cell Neoplasia
PhasePhase 1/2
SponsorSanofi
StatusTerminated
Enrollment101 participants
InterventionsSAR443579
Start dateDec 8, 2021
Completion dateJun 13, 2025
Results postedJul 6, 2026

Summary

This is an open-label, multicenter, Phase 1/Phase 2, dose escalation and dose expansion study to evaluate the safety, pharmacokinetics, pharmacodynamics and anti-leukemic activity of SAR443579 in various hematological malignancies.

Dose Escalation: Number of Participants With Dose Limiting Toxicities (DLTs)

Cycle 1 Day 1 up to Cycle 1 Day 28. Each cycle duration in induction period was 28 days. · Participants

Dose Escalation - Adult Arm: SAR443579 10-100 mcg/kg0 Participants
Dose Escalation - Adult Arm: SAR443579 30-300 mcg/kg0 Participants
Dose Escalation - Adult Arm: SAR443579 750 mcg/kg1 Participants
Dose Escalation - Adult Arm: SAR443579 800 mcg/kg0 Participants
Dose Escalation - Adult Arm: SAR443579 100-1000 mcg/kg0 Participants
Dose Escalation - Adult Arm: SAR443579 300-1000 mcg/kg0 Participants

Dose Escalation (Cohort C): Number of Participants With Dose Limiting Toxicities

Cycle 1 Day 1 to Cycle 1 Day 28. Each cycle duration in induction period was 28 days.

Dose Expansion (Cohorts A1, A2 and D): Composite Complete Remission (CRc) Rate

Tumors were assessed on Day 28 of each induction cycle and Day 56 of each maintenance cycle until disease relapse, unacceptable AE, discontinuation, or death, whichever occurred first. Maximum treatment duration was 20.9 weeks. · percentage of participants

Dose Expansion - Adult Arm (Cohort A1): SAR443579 1000 mcg/kg5.0 percentage of participants

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